This narrative review reports recent advances in transfusion medicine, encompassing enhancements in molecular diagnostics, blood engineering, and therapeutic technologies. It summarizes findings from ...
– 53.7% mean splicing correction observed following a single 15 mg/kg dose of PGN-EDODM1, with all patients showing an improvement in splicing – – PGN-EDODM1 was generally well-tolerated at 15 mg/kg, ...
Breakthroughs, discoveries, and DIY tips sent every weekday. Terms of Service and Privacy Policy. Most of us have heard of pimple patches, those circular bandage-like ...
Discover the biological significance of hidden RNAs and learn how to detect them in RNA-Seq data using advanced techniques.
Biogen to drive end-to-end development and commercialization of ThecaFlex DRx™, an investigational implantable device for intrathecal delivery of antisense oligonucleotides (ASOs) ThecaFlex DRx™ has ...