SAVANNAH, Ga. -- Delandistrogene moxeparvovec (Elevidys), a gene therapy approved to treat Duchenne muscular dystrophy, ...

The Killian family, of Rockwall, are celebrating a record-breaking fundraising milestone with their annual Sam's Night event, ...

A Pfizer result is unsettling the gene therapy push for Duchenne muscular dystrophy: The boys didn't improve even though a ...

Jefferies initiates buy coverage on Sarepta Therapeutics (SRPT) due to Duchenne muscular dystrophy franchise and strong ...

A Phase 3 clinical trial investigating Elevidys (delandistrogene moxeparvovec), a gene therapy for Duchenne muscular ...

A TEEN has spent the last 10 years in a wheelchair after he was diagnosed with a rare genetic muscular disease known as ...

EMA re-confirms non-renewal of conditional marketing authorisation of Duchenne muscular dystrophy medicine, Translarna: Amsterdam, The Netherlands Monday, October 21, 2024, 10:00 ...

Pfizer has told 75 employees in Sanford, North Carolina, that their positions have been eliminated. | Pfizer has told 75 ...

The agency has reconfirmed its recommendation to not give positive opinion to Translarna (ataluren) after a reexamination of the available data.

We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...

In 2020, Zander Teubes, aka ‘Zan the Man’, was diagnosed with Duchenne muscular dystrophy, which causes skeletal and heart muscle weakness and progressively worsens. He needs a wheelchair to move ...

Deep-pocketed investors have adopted a bearish approach towards Capricor Therapeutics CAPR, and it's something market players ...