October is Rett Syndrome Awareness Month. Rett Syndrome is a complex neurological disorder that mainly affects girls in a variety of racial and ethnic groups worldwide. Rett syndrome (RS) is often ...

A University of Virginia School of Medicine scientist is developing an innovative gene therapy she hopes will slow disease progression and improve movement, coordination and communication in children ...

Patients and families facing a Rett syndrome diagnosis experience an array of burdens. Paige Nues: The treatment burden of Rett syndrome is complex. It’s one of the most pervasive, severe neurologic ...

David Lieberman, MD, PhD, describes Rett syndrome, including the various stages, incidence, and potential causes of this disease. David Lieberman, MD, PhD: Rett syndrome is a neurodevelopmental ...

In a comprehensive preclinical program, NGN-401 demonstrated robust therapeutic and safety benefits, delivering MECP2 to key brain regions affected by Rett syndrome NGN-401 utilizes Neurogene’s ...