New preclinical data after neonatal administration in wild-type mice showed no detectable impact on survival, neurobehavioral functions and overall health, suggesting TSHA-102, engineered with novel ...
In a comprehensive preclinical program, NGN-401 demonstrated robust therapeutic and safety benefits, delivering MECP2 to key brain regions affected by Rett syndrome NGN-401 utilizes Neurogene’s ...
Rett syndrome is a rare devastating neurological disorder that primarily affects young girls and manifests as an impaired ability to walk and talk, along with characteristic 'hand-wringing' movements, ...
Rett syndrome is a rare devastating neurological disorder that primarily affects young girls and manifests as an impaired ability to walk and talk, along with characteristic 'hand-wringing' movements, ...
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