University of Utah and Primary Children’s Hospital have created a FXS clinic to care for patients and families living with Fragile X. Our clinic serves the children of Utah and surrounding states ...

Still, like many parents and caregivers of individuals with Fragile X — the most common inherited form of autism and it is one of the most common inherited causes of developmental and intellectual ...

Scientists have created a new therapeutic approach for testing fragile X syndrome, which is the most common genetic cause of autism spectrum disorder (ASD). This method aims to alter a type of neural ...

Please provide your email address to receive an email when new articles are posted on . The FDA has cleared an investigational new drug application for a small molecule therapeutic to treat those with ...

Mirum Pharmaceuticals MIRM announced that it has enrolled the first patient in the phase II BLOOM study evaluating its newly ...

Building on more than two decades of research, a study by MIT neuroscientists at The Picower Institute for Learning and Memory reports a new way to treat pathology and symptoms of fragile X syndrome, ...

In a comprehensive Genomic Press Interview, researchers from the University of Texas Health Science Center at San Antonio and Hirosaki University have uncovered critical new insights into the ...

For 22 years, Jason Mazzola's life was defined by Fragile X, a genetic condition that often causes autism and intellectual disability. Jason, who is 24 now, needed constant supervision. He had ...

Please provide your email address to receive an email when new articles are posted on . The FDA has granted fast-track designation to an investigational small molecule to treat individuals with ...

PLYMOUTH MEETING, Pa.--(BUSINESS WIRE)--Harmony Biosciences Holdings, Inc. (Nasdaq: HRMY), today announced topline results from its Phase 3 registrational clinical trial (the RECONNECT Study) of ...

Detailed price information for Mirum Pharmaceuticals Inc (MIRM-Q) from The Globe and Mail including charting and trades.